CME Presentations

Duchenne Muscular Dystrophy – An Expanding Lifespan


Presentations


Speakers

  • John F. Brandsema, MD

    John F. Brandsema, MD

    John F. Brandsema, MD

    Assistant Professor Of Clinical Neurology

    John F. Brandsema, MD, is an assistant professor of clinical neurology at The Perelman School of Medicine, University of Pennsylvania in Philadelphia, and an attending physician in neuromuscular/ general neurology & electromyography at the Children’s Hospital of Philadelphia (CHOP). He earned his medical degree at Dalhousie University, Halifax, Nova Scotia, Canada and completed his pediatric neurology residency at The Hospital for Sick Children in Toronto, followed by the Partners Neuromuscular Fellowship at Harvard Medical School in Boston, Massachusetts. Dr Brandsema’s broad clinical and research interests is in neuromuscular diseases, with a focus in clinical trials of novel therapies for childhood neuromuscular disorders.
  • Betty Vertin

    Betty Vertin

    Betty Vertin

    Parent of Children with DMD

    Betty Vertin is a married mother of 6 who lives in Hastings, Nebraska. She has an undergraduate degree from Hastings College and a master’s degree from Doane University in Crete, Nebraska. Mrs. Vertin worked in education and with other nonprofit organizations for 10 years. After 3 of her children were diagnosed with Duchenne muscular dystrophy (DMD), her life changed. She now advocates on behalf of her children and all children living with DMD, and often writes about her family’s experiences in her blog, Weathered-Storms.
  • Richard J. Barohn, MD

    Richard J. Barohn, MD

    Richard J. Barohn, MD

    Gertrude and Dewey Ziegler Professor of Neurology

    Richard J. Barohn, MD, is the vice chancellor for research at the University of Kansas Medical Center (KUMC) in Kansas City, the Gertrude and Dewey Ziegler Professor of Neurology and University Distinguished Professor, and the president of the KUMC Research Institute. He is Director of Frontiers: University of Kansas Clinical and Translational Science Institute, where he works to accelerate clinical and translational research at KUMC, in the region, and nationally. Dr Barohn’s research focuses on myopathies, motor neuron diseases, peripheral neuropathies, and myasthenia gravis. He is the author of more than 250 articles, has mentored over 200 neurology residents and fellows, a member of numerous professional societies, and continues to see patients in the neurology clinic.
  • Kathryn R. Wagner, MD, PhD

    Kathryn R. Wagner, MD, PhD

    Kathryn R. Wagner, MD, PhD

    Professor of Pediatrics

    Kathryn R. Wagner, MD, PhD, is the director of the Center for Genetic Muscle Disorders at the Kennedy Krieger Institute, and a professor of neurology and neuroscience at the Johns Hopkins School of Medicine in Baltimore, Maryland She received her BS from Yale University in New Haven, Connecticut, and her and MD and PhD from the Johns Hopkins School of Medicine. Dr Wagner's work focuses on muscle regeneration and therapeutic development for the muscular dystrophies. She is a scientific advisor for the FSH Society, Parent Project Muscular Dystrophy, and the TREAT-NMD Advisory Committee for Therapeutics, and is an elected member of American Society for Clinical Investigation.
  • Oscar H. Mayer, MD

    Oscar H. Mayer, MD

    Oscar H. Mayer, MD

    Associate Professor of Clinical Pediatrics

    Oscar H. Mayer, MD, is a professor of clinical pediatrics at The Perelman School of Medicine at the University of Pennsylvania in Philadelphia, an attending pulmonologist within the Division of Pulmonology at the Children’s Hospital of Philadelphia (CHOP) and is the medical director of the CHOP pulmonary function testing laboratory. He is the pulmonologist in the Neuromuscular Center and the Center for Thoracic Insufficiency Syndrome and directs the management of outpatients and inpatients. Dr Mayer’s clinical interests include managing patients with chronic respiratory failure, the pulmonary manifestations of neuromuscular disease, and assessing and managing patients with complex chest wall and spine disease. He is an active member of CHOP’s Asthma Clinical Science and Research and Group.

CME Information

Duchenne Muscular Dystrophy – An Expanding Lifespan


  

LEARNING OBJECTIVES

At the conclusion of this activity, participants will be able to:

  • Summarize the differential diagnosis of DMD and applicable diagnostic approaches
  • Adopt a multidisciplinary approach to diagnosing patients with DMD
  • Describe signs and symptoms that would raise a high index of suspicion of DMD
  • Identify mutations that may be associated with DMD and how that relates to making treatment decisions
  • Assess the therapeutic potential of available and emerging treatment options for the management of DMD
  • Adopt a multidisciplinary approach to managing patients with DMD
  • Describe elements for a successful transition from childhood to adulthood care in patients with DMD

Acknowledgement

This activity is supported by educational grants from Sarepta and PTC Therapeutics.

Tuition

Complimentary

JOINT ACCREDITATION STATEMENT

In support of improving patient care, this activity has been planned and implemented by the Postgraduate Institute for Medicine and PlatformQ Health Education, LLC. Postgraduate Institute for Medicine is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.

Credit Designation Statements

Live Internet Activity

The Postgraduate Institute for Medicine designates this live activity for a maximum of 2.0 AMA PRA Category 1 Credit(s)™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

Enduring Material

The Postgraduate Institute for Medicine designates this enduring material for a maximum of 2.0 AMA PRA Category 1 Credit(s)™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

Date of Releasae/Expiration

Live Activity
Wednesday, March 20, 2019 from 12:30pm – 2:30pm EST.

Enduring Material
The enduring material will be available from March 20, 2019 to March 20, 2020.

Target Audience

This activity is intended for pediatricians, neurologists, neuromuscular specialists, endocrinologists, gastroenterologists, pediatric cardiologists, physiatrists, pulmonologists, pediatric neurologists, primary care physicians, advanced practitioners, pharmacists, nurses, and dieticians.

Estimated Time to Complete

This activity consists of one session which should take approximately 2 hour to complete.

Method of Participation

There are no fees to participate in this activity. To participate in the activity, go to www.NeuroSeriesLive.com. To receive credit, participants must (1) read the target audience, learning objectives, and disclosure statements, (2) complete the educational activity online, and (3) complete the post-test and activity evaluation. To receive AMA PRA Category 1 Credits™, participants must receive a minimum score of 70% on the post-test.

Hardware/Software Requirements

Participants will need a computer with a recent version of Adobe Flash installed, as well as an internet connection sufficient for streaming media.

Disclosure of Conflicts of Interest

Postgraduate Institute for Medicine (PIM) requires instructors, planners, managers and other individuals who are in a position to control the content of this activity to disclose any real or apparent conflict of interest (COI) they may have as related to the content of this activity. All identified COI are thoroughly vetted and resolved according to PIM policy. PIM is committed to providing its learners with high quality CME activities and related materials that promote improvements or quality in healthcare and not a specific proprietary business interest of a commercial interest.

The faculty reported the following financial relationships or relationships to products or devices they or their spouse/life partner have with commercial interests related to the content of this CME activity:

Financial Disclosures

Presenters

Richard J. Barohn, MD

Consulting Fees: NuFactor, Momenta Pharma
Contracted Research: PTC Therapeutics, Ra Pharma, Orphazyme, Sanofi Genzyme, NIH, PCORI

John F. Brandsema, MD

Consulting Fees: Biogen, AveXis, PTC Therapeutics, Sarepta, Alexion, Cytokinetics
Fees for Non-CME/CE Services Received Directly from a Commercial Interest: Biogen
Contracted Research: Biogen, AveXis, PTC Therapeutics, Sarepta, Alexion, Cytokinetics

Kathryn R. Wagner, MD, PhD

Consulting Fees: Lion, Sarepta, PTC, Wave, Fibrogen
Contracted Research: Pfizer, Sarepta, Catabasis, Roche

Oscar H. Mayer, MD

Fees for Non-CME/CE Services Received Directly from a Commercial Interest: PTC Therapeutics (educational presentation for employees)

Betty Vertin

Salary (Spouse): Stellar Industries

The planners and managers reported the following financial relationships or relationships to products or devices they or their spouse/life partner have with commercial interests related to the content of this CME activity:

Financial Disclosures

David Howard
Medical Director
PlatformQ Health Education, LLC
Reported Financial Relationship: None

The PIM planners and managers have nothing to disclose.

The following PlatformQ Health Education, LLC planner, Elizabeth del Nido, hereby states that she or her spouse/life partner do not have any financial relationships or relationships to products or devices with any commercial interest related to the content of this activity of any amount during the past 12 months.

Disclosure of Unapproved/Off Label Use (if applicable):

This educational activity may contain discussion of published and/or investigational uses of agents that are not indicated by the FDA. The planners of this activity do not recommend the use of any agent outside of the labeled indications.

The opinions expressed in the educational activity are those of the faculty and do not necessarily represent the views of the planners. Please refer to the official prescribing information for each product for discussion of approved indications, contraindications, and warnings.

Discalimer

Participants have an implied responsibility to use the newly acquired information to enhance patient outcomes and their own professional development. The information presented in this activity is not meant to serve as a guideline for patient management. Any procedures, medications, or other courses of diagnosis or treatment discussed or suggested in this activity should not be used by clinicians without evaluation of their patient’s conditions and possible contraindications and/or dangers in use, review of any applicable manufacturer’s product information, and comparison with recommendations of other authorities.

Contact Information

Accreditation Support:
Please contact the Postgraduate Institute for Medicine at www.pimed.com

Technical Support:
For any technical issues or issues with your CME Certificate, please contact NeuroSeriesLive at 877-394-1306 or at Support@NeuroSeriesLive.com